Haematopoietic gene therapy of non-conditioned patients with Fanconi anaemia-A: results from open-label phase 1/2 (FANCOLEN-1) and long-term clinical trials

Paula Rı́o, Josune Zubicaray, Susana Navarro, Eva Heredero Gálvez, Rebeca Sánchez‐Domínguez, Eileen Nicoletti, Elena Sebastián, Michael Rothe, Roser Pujol, Massimo Bogliolo, Philipp John-Neek, Antonella Lucía Bastone, Axel Schambach, Wei Wang, Manfred Schmidt, Lise Larcher, José C. Segovia, Rosa María Pérez Yáñez, Omaira Alberquilla, Begoña Díez, María Fernández-García, Laura García‐García, Manuel Ramı́rez, Anne Galy, François Lefrère, Marina Cavazzana, Thierry Leblanc, Nagore García de Andoín, Ricardo López Almaraz, Albert Català, Jordi Barquinero, Sandra Rodríguez, Gayatri R Rao, Jordi Surrallés, Jean Soulier, Cristina Díaz de Heredia, Jonathan D. Schwartz, Julián Sevilla, Juan A. Bueren, Paula Río, Josune Zubicaray, Susana Navarro, Eva Gálvez, Rebeca Sánchez-Domínguez, Eileen Nicoletti, Elena Sebastián, Michael Rothe, Roser Pujol, Massimo Bogliolo, Philipp John-Neek, Antonella L Bastone, Axel Schambach, Wei Wang, Manfred Schmidt, Lise Larcher, José C Segovia, Rosa M Yáñez, Florencio Pérez-Maroto, Ana de la Cruz, José A Casado, Yari Giménez, Lara Álvarez, Omaira Alberquilla, Begoña Díez, María Fernández-García, Laura García-García, Ana Gómez, Almudena Galán, Manuel Ramírez, Rocío Salgado, Anne Galy, Francois Lefrere, Marina Cavazzana, Thierry Leblanc, Nagore Garcia de Andoin, Ricardo López-Almaraz, Albert Catalá, Jordi Barquinero, Sandra Rodríguez-Perales, Gayatri Rao, Jordi Surrallés, Jean Soulier, Cristina Díaz-de-Heredia, Jonathan D Schwartz, Julián Sevilla, Juan A Bueren