A review of the rationale for gene therapy for hemophilia A with inhibitors: one-shot tolerance and treatment?
Leonard A. Valentino, Margareth C. Ozelo, Roland W. Herzog, Nigel S. Key, Allyson M. Pishko, Margaret V. Ragni, Benjamin J. Samelson‐Jones, David Lillicrap
Topics & Concepts
MedicineGenetic enhancementImmunologyGeneBiologyGeneticsHemophilia Treatment and Research