Next-generation biological vector platforms for in vivo delivery of genome editing agents
Delphine Leclerc, Michael Siroky, Shannon M. Miller
Topics & Concepts
Genome editingCRISPRComputational biologyIn vivoTransduction (biophysics)GenomeGenetic enhancementBiologyEx vivoGenome engineeringGene deliveryGeneGeneticsBiochemistryCRISPR and Genetic EngineeringVirus-based gene therapy researchRNA Interference and Gene Delivery