Peripheral blood stem and progenitor cell collection in pediatric candidates for ex vivo gene therapy: a 10-year series
Daniele Canarutto, Francesca Tucci, Salvatore Gattillo, Matilde Zambelli, Valeria Calbi, Bernhard Gentner, Francesca Ferrua, Sarah Marktel, Maddalena Migliavacca, Federica Barzaghi, Giulia Consiglieri, Vera Gallo, Francesca Fumagalli, Paola Massariello, Cristina Parisi, Gianluca Viarengo, Elena Albertazzi, Paolo Silvani, Raffaella Milani, Luca Santoleri, Fabio Ciceri, Maria Pia Cicalese, Maria Ester Bernardo, Alessandro Aiuti
Abstract
cell yields for the purpose of GT, with a favorable safety profile.
Topics & Concepts
Progenitor cellCD34MedicinePlerixaforBone marrowStem cellEx vivoGenetic enhancementHaematopoiesisLeukapheresisImmunologyOncologyInternal medicineIn vivoBiologyCXCR4Cell biologyBiotechnologyGeneChemokineBiochemistryImmune systemVirus-based gene therapy researchCAR-T cell therapy researchHematopoietic Stem Cell Transplantation