Trofinetide for the treatment of Rett syndrome: Long-term safety and efficacy results of the 32-month, open-label LILAC-2 study
Alan K. Percy, Jeffrey L. Neul, Tim A. Benke, Elizabeth Berry‐Kravis, Daniel G. Glaze, Eric D. Marsh, Amy Barrett, Di An, Kathie M. Bishop, James M. Youakim
Topics & Concepts
lilacTerm (time)Rett syndromeOpen labelMedicinePharmacologyAdverse effectChemistryBiologyHorticulturePhysicsBiochemistryQuantum mechanicsGeneGenetics and Neurodevelopmental DisordersChild Nutrition and Feeding IssuesFamily and Disability Support Research