Bone-marrow-homing lipid nanoparticles for genome editing in diseased and malignant haematopoietic stem cells
Xizhen Lian, Sumanta Chatterjee, Yehui Sun, Sean A. Dilliard, Stephen D. Moore, Yufen Xiao, Xiaoyan Bian, Kohki Yamada, Yun‐Chieh Sung, Rachel M. Levine, Kalin Mayberry, Samuel John, Xiaoye Liu, Caroline Smith, Lindsay T. Johnson, Xu Wang, Cheng Cheng Zhang, David R. Liu, Gregory A. Newby, Mitchell J. Weiss, Jonathan Yen, Daniel J. Siegwart
Topics & Concepts
Homing (biology)HaematopoiesisStem cellBone marrowNanoparticleCell biologyBiologyCancer researchNanotechnologyMaterials scienceImmunologyEcologyCRISPR and Genetic EngineeringRNA Interference and Gene DeliveryVirus-based gene therapy research