Hemophilia Gene Therapy Value Assessment: Methodological Challenges and Recommendations
Louis P. Garrison, Ed Pezalla, Adrian Towse, Hongbo Yang, Elizabeth Faust, Eric Q. Wu, Nanxin Li, Eileen K. Sawyer, Michael Recht
Topics & Concepts
MedicineQuality of life (healthcare)Valuation (finance)Cost–benefit analysisValue (mathematics)Clinical trialQuality-adjusted life yearCost effectivenessIntensive care medicineHealth careEconomic evaluationRisk analysis (engineering)Computer scienceBusinessEconomicsFinancePathologyNursingMachine learningEconomic growthEcologyBiologyCAR-T cell therapy researchHemophilia Treatment and Research