AAV gene therapy for Tay-Sachs disease

Terence R. Flotte, Oğuz Çataltepe, Ajit S Puri, Ana Rita Batista, Richard P. Moser, Diane McKenna‐Yasek, Catherine Douthwright, Gwladys Gernoux, Meghan Blackwood, Christian Mueller, Phillip W.L. Tai, Xuntian Jiang, Scot T. Bateman, Spiro G. Spanakis, Julia Parzych, Allison M. Keeler, Aly Abayazeed, Saurabh Rohatgi, Laura Gibson, Robert W. Finberg, Bruce Barton, Zeynep Vardar, Mohammed Salman Shazeeb, Matthew J. Gounis, Cynthia J. Tifft, Florian Eichler, Robert H. Brown, Douglas R. Martin, Heather Gray‐Edwards, Miguel Sena‐Esteves