Hematopoietic Stem Cell Transplantation in ARPC1B Deficiency
Stefano Giardino, Stefano Volpi, Federica Lucioni, Roberta Caorsi, Jennifer Schneiderman, Abigail Lang, Amer Khojah, Taco W. Kuijpers, Ionanna Papadatou, Anna Paisiou, Laura Alonso, Ansgar Schulz, Nufar Marcus, Marco Gattorno, Maura Faraci
Topics & Concepts
MedicineHematopoietic stem cell transplantationPrimary immunodeficiencyFailure to thriveThrombotic microangiopathyTransplantationSevere combined immunodeficiencyWiskott–Aldrich syndromeImmunodeficiencyGraft-versus-host diseaseProgressive multifocal leukoencephalopathyInternal medicineDiseaseImmunologyGastroenterologyPediatricsImmune systemVirusGeneChemistryBiochemistryImmunodeficiency and Autoimmune DisordersParvovirus B19 Infection StudiesPolyomavirus and related diseases