iPSC modeling of young-onset Parkinson’s disease reveals a molecular signature of disease and novel therapeutic candidates
Alex Laperle, Samuel Sances, Nur Yucer, Victoria Dardov, Veronica J. Garcia, Ritchie Ho, AnneB Fulton, Michelle R. Jones, Kristina Roxas, Pablo Avalos, Destiny West, Maria G. Bañuelos, Zhan Shu, Ramachandran Murali, Nigel T. Maidment, Jennifer E. Van Eyk, Michele Tagliati, Clive N. Svendsen
Topics & Concepts
Induced pluripotent stem cellBiologyAlpha-synucleinCell biologyDopaminergicParkinson's diseaseDiseaseDopamineGeneMedicineGeneticsInternal medicineEndocrinologyEmbryonic stem cellParkinson's Disease Mechanisms and TreatmentsNuclear Receptors and SignalingCRISPR and Genetic Engineering