Gene therapy for X-linked severe combined immunodeficiency: Historical outcomes and current status
Sung‐Yun Pai, Adrian J. Thrasher
Topics & Concepts
Severe combined immunodeficiencyCommon gamma chainImmune systemHematopoietic stem cell transplantationImmunodeficiencyImmunologyMedicinePrimary immunodeficiencyStem cellImmunityGenetic enhancementLymphocyteTransplantationHaematopoiesisCytokineBiologyInternal medicineGeneInterleukin 10GeneticsImmunodeficiency and Autoimmune DisordersVirus-based gene therapy researchCAR-T cell therapy research