Utilization of a novel Sendai virus vector in ex vivo gene therapy for hemophilia A
Yuni Yamaki, Takashi Fukushima, Naomi Yoshida, Ken Nishimura, Aya Fukuda, Koji Hisatake, Masayuki Aso, Tomoki Sakasai, Junko Kijima-Tanaka, Yoshihiro Miwa, Mahito Nakanishi, Ryo Sumazaki, Hidetoshi Takada
Topics & Concepts
Sendai virusVector (molecular biology)Genetic enhancementTransfectionVirologyViral vectorIn vivoEx vivoBiologyTransplantationVirusImmunologyGeneMolecular biologyMedicineGeneticsInternal medicineRecombinant DNAVirus-based gene therapy researchViral Infectious Diseases and Gene Expression in InsectsHemophilia Treatment and Research