Fitusiran in haemophilia: a breakthrough drug with many unknowns
Flora Peyvandi, Isabella Garagiola, Maria R. Abbattista
Topics & Concepts
HaemophiliaHaemophilia BMedicineHaemophilia AFactor IXAntithrombinHemostasisInternal medicinePediatricsPharmacologyHeparinHemophilia Treatment and ResearchBlood Coagulation and Thrombosis MechanismsCancer-related gene regulation