Approaches to Gene Modulation Therapy for ALS
Katharina E. Meijboom, Robert H. Brown
Topics & Concepts
Amyotrophic lateral sclerosisAdeno-associated virusGenetic enhancementSOD1Gene silencingMedicineDiseaseC9orf72NeuroscienceGeneBioinformaticsBiologyGeneticsPathologyFrontotemporal dementiaVector (molecular biology)DementiaRecombinant DNAAmyotrophic Lateral Sclerosis ResearchNeurogenetic and Muscular Disorders ResearchPrion Diseases and Protein Misfolding