Litcius/Paper detail

RNA-targeted drugs for neuromuscular diseases

Alessandra Ferlini, Aurélie Goyenvalle, Francesco Muntoni

2020Science26 citationsDOI

Abstract

Progress with antisense oligonucleotide therapies opens a path for future development

Topics & Concepts

RNAMedicineComputational biologyPharmacologyBiologyGeneticsGeneNeurogenetic and Muscular Disorders ResearchRNA Research and SplicingViral Infections and Immunology Research
RNA-targeted drugs for neuromuscular diseases | Litcius