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Antisense oligonucleotides enhance SLC20A2 expression and suppress brain calcification in a humanized mouse model

Miao Zhao, Xuewen Cheng, Lei Chen, Yi‐Heng Zeng, Kai-Jun Lin, Yun‐Lu Li, Ze-Hong Zheng, Huang Xue-jing, Dandan Zuo, Xin-Xin Guo, Jun Guo, Dian He, Ying Liu, Yu Lin, Chong Wang, Wenqi Lv, Hui‐Zhen Su, Xiang‐Ping Yao, Zi-Ling Ye, Xiaohong Chen, Ying‐Qian Lu, Chen‐Wei Huang, Guang Yang, Yuxian Zhang, Min‐Ting Lin, Ning Wang, Zhi‐Qi Xiong, Wan‐Jin Chen

2024Neuron23 citationsDOIOpen Access PDF

Topics & Concepts

NeuroscienceOligonucleotideHumanized mouseCalcificationBiologyPsychologyGeneMedicineGeneticsIn vivoPathologyGenetic Syndromes and ImprintingNeurogenetic and Muscular Disorders ResearchMetalloenzymes and iron-sulfur proteins
Antisense oligonucleotides enhance SLC20A2 expression and suppress brain calcification in a humanized mouse model | Litcius