RNA-targeting and gene editing therapies for transthyretin amyloidosis
Alberto Aimo, Vincenzo Castiglione, Claudio Rapezzi, Maria Franzini, Giorgia Panichella, Giuseppe Vergaro, Julian D. Gillmore, Marianna Fontana, Claudio Passino, Michele Emdin
Topics & Concepts
TransthyretinAmyloidosisCardiomyopathyPolyneuropathyMedicineSmall interfering RNACancer researchAmyloid (mycology)Gene silencingGeneBioinformaticsBiologyRNAHeart failurePathologyInternal medicineGeneticsAmyloidosis: Diagnosis, Treatment, OutcomesEosinophilic Disorders and SyndromesCardiomyopathy and Myosin Studies