The role of haematopoietic stem cell transplantation for sickle cell disease in the era of targeted disease-modifying therapies and gene editing
Josu de la Fuente, Éliane Gluckman, Julie Makani, Paul Telfer, Lawrence Faulkner, Selim Corbacioglu, Persis Amrolia, Marc Ansari, Adriana Balduzzi, Arnaud Dalassier, Jean‐Hugues Dalle, Cristina Hereda Diaz, Tobias Feuchtinger, Franco Locatelli, Giovanna Lucchini, Jaques-Emmanuel Galimard, Marta González Vincent, Rupert Handgretinger, Katharina Kleinschmidt, Ánita Lawitschka, A. Pérez Martínez, Christina Peters, Vanderson Rocha, Annalisa Ruggeri, Petr Sedláček, Peter Švec, Jacek Toporski, Akif Yeşilipek
Topics & Concepts
MedicineDiseaseTransplantationStem cellHaematopoiesisHematopoietic stem cell transplantationIntensive care medicineImmunologyPediatricsInternal medicineBiologyGeneticsHemoglobinopathies and Related DisordersPrenatal Screening and DiagnosticsParvovirus B19 Infection Studies