Litcius/Paper detail

Treating sickle cell anemia

John F. Tisdale, Swee Lay Thein, William A. Eaton

2020Science81 citationsDOIOpen Access PDF

Abstract

New drugs, stem cell transplants, and gene therapy show promise in treating sickle cell anemia

Topics & Concepts

Sickle cell anemiaCellAnemiaGenetic enhancementMedicineStem cellBiologyGeneInternal medicineGeneticsHemoglobinopathies and Related DisordersIron Metabolism and DisordersErythrocyte Function and Pathophysiology