Focused Update on AAV-Based Gene Therapy Clinical Trials for Inherited Retinal Degeneration
Paula Fuller-Carter, Hamed Basiri, Alan R. Harvey, Lívia S. Carvalho
Topics & Concepts
Clinical trialMedicineGenetic enhancementAdeno-associated virusBioinformaticsIntensive care medicineNeurosciencePathologyGeneBiologyVector (molecular biology)GeneticsRecombinant DNARetinal Development and DisordersVirus-based gene therapy researchRetinal and Optic Conditions