Litcius/Paper detail

Recessively Inherited Deficiency of Secreted WFDC2 (HE4) Causes Nasal Polyposis and Bronchiectasis

Gerard W. Dougherty, Lawrence E. Ostrowski, Tabea Nöthe-Menchen, Johanna Raidt, Andre Schramm, Heike Olbrich, Weining Yin, Patrick R. Sears, Hong Dang, Amanda Smith, Achim G. Beule, Rim Hjeij, Niels W. Rutjes, Eric G. Haarman, Saskia M. Maas, Thomas W. Ferkol, Peadar G. Noone, Kenneth N. Olivier, Diana Bracht, Pascal Barbry, Laure‐Emmanuelle Zaragosi, Morgane Fierville, Sabine Kliesch, Kai Wohlgemuth, Julia König, Sebastian George, Niki T. Loges, Agathe Ceppe, Matthew R. Markovetz, Hong Luo, Ting Guo, Hoda Rizk, Tarek El-Desoky, Katrin Dahlke, Karsten Boldt, Marius Ueffing, David B. Hill, Yuan‐Ping Pang, Michael R. Knowles, Maimoona A. Zariwala, Heymut Omran

2024American Journal of Respiratory and Critical Care Medicine15 citationsDOIOpen Access PDF

Abstract

dysfunction defines a novel molecular etiology of bronchiectasis characterized by the deficiency of a secreted component of the airways. A commercially available blood test combined with genetic testing allows its diagnosis.

Topics & Concepts

BronchiectasisPrimary ciliary dyskinesiaMedicineCystic fibrosisImmunologySalivaMucociliary clearanceSanger sequencingPathologyLungBiologyMutationGeneGeneticsInternal medicineCystic Fibrosis Research AdvancesNeonatal Respiratory Health ResearchTracheal and airway disorders