Litcius/Paper detail

Spinal Muscular Atrophy

Stefan Nicolau, Megan A. Waldrop, Anne M. Connolly, Jerry R. Mendell

2021Seminars in Pediatric Neurology81 citationsDOI

Topics & Concepts

Spinal muscular atrophyMedicineAtrophyDiseaseMuscle atrophyIntensive care medicinePhysical medicine and rehabilitationNeuromuscular diseaseGenetic enhancementPhysical therapyBioinformaticsPathologyChemistryGeneBiologyBiochemistryNeurogenetic and Muscular Disorders ResearchCongenital Anomalies and Fetal SurgeryRNA modifications and cancer