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A Phase II prospective trial of azacitidine in steroid-dependent or refractory systemic autoimmune/inflammatory disorders and VEXAS syndrome associated with MDS and CMML

A. Mékinian, Lin‐Pierre Zhao, Sylvie Chevret, Kristell Desseaux, Laurent Pascal, Thibaut Comont, A. Maria, Pierre Péterlin, Louis Terriou, Maud D’Aveni Piney, Marie-Pierre Gourin, Norbert Vey, Odile Beyne Rauzy, Vincent Grobost, H. Bézanahary, Sophie Dimicoli‐Salazar, Anne Banos, Stefan Wickenhauser, Benoît De Renzis, Éric Durot, Shanti Natarajan‐Amé, Laurent Voillat, Fatiha Chermat, Karine Lemaire, Vincent Jachiet, Chantal Himberlin, Sylvain Thépot, José Miguel Torregrosa Diaz, Laurent Frenzel, Emmanuel Gyan, Guillaume Denis, Pierre Hirsch, Olivier Kosmider, Lionel Adès, O. Fain, Pierre Fenaux

2022Leukemia92 citationsDOI

Topics & Concepts

AzacitidineMedicineRefractory (planetary science)Internal medicineImmunologyClinical trialOncologyBiologyBiochemistryAstrobiologyDNA methylationGene expressionGeneOtitis Media and Relapsing PolychondritisVascular Anomalies and TreatmentsHistiocytic Disorders and Treatments
A Phase II prospective trial of azacitidine in steroid-dependent or refractory systemic autoimmune/inflammatory disorders and VEXAS syndrome associated with MDS and CMML | Litcius