Familial Hypercholesterolemia
Julia Brandts, Kausik K. Ray
Topics & Concepts
LDL receptorMedicinePCSK9EzetimibeFamilial hypercholesterolemiaGenetic enhancementSmall interfering RNARNA interferenceLoss functionCRISPRTranslation (biology)RNABioinformaticsPhenotypeMessenger RNACholesterolGeneLipoproteinGeneticsInternal medicineBiologyLipoproteins and Cardiovascular HealthCRISPR and Genetic EngineeringLipid metabolism and disorders