Delivery of therapeutic AAV9 vectors via cisterna magna to treat neurological disorders
Paolo Marchi, Lara Marrone, Mimoun Azzouz
Topics & Concepts
Cisterna magnaMedicineSpinal cordAdeno-associated virusCentral nervous systemGene deliveryVector (molecular biology)Systemic administrationGenetic enhancementPharmacologyPathologyCerebrospinal fluidBiologyInternal medicineIn vivoRecombinant DNABiochemistryGeneBiotechnologyPsychiatryVirus-based gene therapy researchNerve injury and regenerationHerpesvirus Infections and Treatments