Litcius/Paper detail

Addition of danicopan to ravulizumab or eculizumab in patients with paroxysmal nocturnal haemoglobinuria and clinically significant extravascular haemolysis (ALPHA): a double-blind, randomised, phase 3 trial

Jong Wook Lee, Morag Griffin, Jin Seok Kim, Lily Wong Lee Lee, Caroline Piatek, Jun‐ichi Nishimura, Cynthia Carrillo Infante, Deepak Jain, Peng Liu, Gleb Filippov, Flore Sicre de Fontbrune, Antonio M. Risitano, Austin Kulasekararaj, Wilma Barcellini, Fiorenza Barraco, David Beneitez Pastor, Marcelo Capra, Lee Ping Chew, Lalayanni Chrysavgi, Lalayanni Chrysavgi, Régis Peffault de la Tour, Michel Michels Oliveira, Eros Di Bona, Édouard Forcade, Chieh‐Lin Fu, Cossor Furha, Anna Gaya Valls, Stavroula Giannouli, Ataúlfo González-Fernández, Morag Griffin, Alexander Gural, Emilio Ojeda Gutierrez, Inés Hernández‐Rodríguez, Ibrahim Ibrahim, Anna Paola Iori, Tadao Ishida, Jun Ho Jang, Jun Ho Jang, Jin Seok Kim, Toshiyuki Kitano, Hiroshi Kosugi, Natalia Kreiniz, Austin Kulasekararaj, Jong Wook Lee, Jong Wook Lee, Jiřı́ Mayer, Lindsay Mitchell, Yasuo Mori, Kaichi Nishiwaki, Rosario Notaro, Ramiro Núñez, Naoshi Obara, Esther Natalie Olíva, Christopher J. Patriquin, Viviani Pessôa, Caroline Piatek, Agnieszka Piekarska, Shahzad Raza, Antonio M. Risitano, Ponlapat Rojnuckarin, Desmond Samuel, Jamile M. Shammo, Tamar Tadmor, Akiyoshi Takami, Roni Tamari, Louis Terriou, Hitoji Uchiyama, Alessandro M. Vannucchi, Hiroki Yamaguchi, Alessandro M. Vannucchi, Hiroki Yamaguchi

2023The Lancet Haematology86 citationsDOI

Topics & Concepts

EculizumabMedicineHaemolysisPlaceboInternal medicineInterim analysisClinical endpointClinical trialSurgeryImmunologyAntibodyPathologyAlternative medicineComplement systemComplement system in diseasesBlood groups and transfusionPlatelet Disorders and Treatments