Advances in Pompe Disease Treatment: From Enzyme Replacement to Gene Therapy
Pasqualina Colella
Topics & Concepts
Enzyme replacement therapyGenetic enhancementHuman geneticsDiseaseMedicineMolecular medicinePharmacotherapyIntensive care medicineGeneBioinformaticsBiologyInternal medicineGeneticsCell cycleLysosomal Storage Disorders ResearchBiochemical and Molecular ResearchTrypanosoma species research and implications