The potential role of miRNA therapies in spinal muscle atrophy
Gayatri Gandhi, Syahril Abdullah, Agus Iwan Foead, Wendy Wai Yeng Yeo
Topics & Concepts
Spinal muscular atrophySMN1SMA*Motor neuronmicroRNANeuroscienceAmyotrophic lateral sclerosisGenetic enhancementBioinformaticsMedicineDiseaseSpinal cordBiologyGenePathologyGeneticsMathematicsCombinatoricsNeurogenetic and Muscular Disorders ResearchCongenital Anomalies and Fetal SurgeryRNA modifications and cancer