Age related treatment effect in type II Spinal Muscular Atrophy pediatric patients treated with nusinersen
Giorgia Coratti, Marika Pane, Simona Lucibello, Maria Carmela Pera, Amy Pasternak, Jacqueline Montes, Valeria Sansone, Tina Duong, Sally Dunaway Young, Sonia Messina, Adele D’Amico, Matthew Civitello, Allan M. Glanzman, Claudio Bruno, Francesca Salmin, Paola Tacchetti, Sara Carnicella, Maria Sframeli, Laura Antonaci, A. Frongia, Darryl C. De Vivo, Basil T. Darras, John Day, Enrico Bertini, Francesco Muntoni, Richard S. Finkel, Eugenio Mercuri
Topics & Concepts
SMA*MedicineNatural historyCohortSpinal muscular atrophyAnalysis of variancePediatricsMultivariate analysisCohort studySurgeryInternal medicineDiseaseCombinatoricsMathematicsNeurogenetic and Muscular Disorders ResearchCardiac Structural Anomalies and RepairMuscle Physiology and Disorders