Early initiation of high-dose oral ambroxol in combination with enzyme replacement therapy in a neuropathic Gaucher infant
Shao‐Yin Chu, Chun-Ching Chien, Wuh‐Liang Hwu, Pen‐Jung Wang, Yin‐Hsiu Chien
Topics & Concepts
AmbroxolMedicineEnzyme replacement therapyPharmacologyInternal medicineAnesthesiaDiseaseLysosomal Storage Disorders ResearchMetabolism and Genetic DisordersCoenzyme Q10 studies and effects