mRNA therapies: Pioneering a new era in rare genetic disease treatment
Guobo Shen, Jian Liu, Hanmei Yang, Na Xie, Yang Yang
Topics & Concepts
Genetic enhancementDiseaseRare diseaseClinical trialMessenger RNAMedicineBioinformaticsComputational biologyBiologyGeneGeneticsPathologyRNA Interference and Gene DeliveryCRISPR and Genetic EngineeringVirus-based gene therapy research