AAV-based in vivo gene therapy for neurological disorders
Qinglan Ling, Jessica A. Herstine, Allison M. Bradbury, Steven J. Gray
Topics & Concepts
Genetic enhancementAdeno-associated virusMedicineTransgeneClinical trialDiseaseVector (molecular biology)BioinformaticsGene deliveryAdverse effectDrug developmentNeuroscienceDrugPharmacologyGeneBiologyPathologyGeneticsRecombinant DNAVirus-based gene therapy researchRNA Interference and Gene DeliveryCRISPR and Genetic Engineering