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AAV-based CRISPR-Cas9 genome editing: Challenges and engineering opportunities

Ami M. Kabadi, Maria Katherine Mejía‐Guerra, John D. Graef, Sohrab Khan, Eric M. Walton, Xinzhu Wang, Charles A. Gersbach, Rachael A. Potter

2023Current Opinion in Biomedical Engineering18 citationsDOI

Topics & Concepts

Genome editingCRISPRCas9Genome engineeringGenomeComputational biologyBiologyGenetic enhancementViral vectorCapsidGene deliveryGeneComputer scienceGeneticsRecombinant DNACRISPR and Genetic EngineeringVirus-based gene therapy researchInnovation and Socioeconomic Development
AAV-based CRISPR-Cas9 genome editing: Challenges and engineering opportunities | Litcius