BBB-crossing adeno-associated virus vector: An excellent gene delivery tool for CNS disease treatment
Wenli Chen, Shun Yao, Jie Wan, Yu Tian, Lan Huang, Shanshan Wang, Farhana Akter, Yinqiu Wu, Yizheng Yao, Xiaochun Zhang
Topics & Concepts
Adeno-associated virusGenetic enhancementCentral nervous systemBlood–brain barrierGene deliveryViral vectorNeuroscienceMedicineBiologyGeneVector (molecular biology)GeneticsRecombinant DNAVirus-based gene therapy researchRNA Interference and Gene DeliveryCRISPR and Genetic Engineering