Litcius/Paper detail

Quinine copolymer reporters promote efficient intracellular DNA delivery and illuminate a protein-induced unpackaging mechanism

Craig Van Bruggen, David Punihaole, Allison Keith, Andrew J. Schmitz, Jakub Tolar, Renee R. Frontiera, Theresa M. Reineke

2020Proceedings of the National Academy of Sciences39 citationsDOIOpen Access PDF

Abstract

-HEA) packages pDNA and shows exceptional cellular internalization, transgene expression, and low cytotoxicity compared to commercial controls for several human cell lines, including HeLa, HEK 293T, K562, and keratinocytes (N/TERTs). Using quinine as an endogenous reporter for pDNA intercalation, Raman imaging revealed that proteins inside cells facilitate the unpackaging of polymer-DNA complexes (polyplexes) and the release of their cargo. Our work showcases the ability of this quinine copolymer reporter to not only facilitate effective gene delivery but also enable diagnostic monitoring of polymer-pDNA binding interactions on the molecular scale via Raman imaging. The use of Raman chemical imaging in the field of gene delivery yields unprecedented insight into the unpackaging behavior of polyplexes in cells and provides a methodology to assess and design more efficient delivery vehicles for gene-based therapies.

Topics & Concepts

Nucleic acidQuinineGene deliveryDNAPolymerIntracellularNanotechnologyChemistryBiophysicsCell biologyGenetic enhancementBiochemistryGeneBiologyMaterials scienceOrganic chemistryMalariaImmunologyRNA Interference and Gene DeliveryAdvanced biosensing and bioanalysis techniquesVirus-based gene therapy research