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Pathogenesis and therapeutic targets in spinal muscular atrophy (SMA)

S. Lefebvre, Catherine Sarret

2020Archives de Pédiatrie21 citationsDOI

Topics & Concepts

SMN1Spinal muscular atrophySMA*Motor neuronBiologySpinal cordNeuroscienceAtrophyBioinformaticsGeneGeneticsMathematicsCombinatoricsNeurogenetic and Muscular Disorders ResearchRNA modifications and cancerRNA Research and Splicing
Pathogenesis and therapeutic targets in spinal muscular atrophy (SMA) | Litcius