Litcius/Paper detail

<i>CALR</i> mutation burden in essential thrombocythemia and disease outcome

Paola Guglielmelli, Natasha Szuber, Naseema Gangat, Giulio Capecchi, Chiara Maccari, Michaël Harnois, Omer Karrar, Maymona Abdelmagid, Manjola Balliu, Elena Nacca, Alessandro Atanasio, Ilaria Sestini, Audrey Désilets, Giuseppe Gaetano Loscocco, Giada Rotunno, Lambert Busque, Ayalew Tefferi, Alessandro M. Vannucchi

2024Blood12 citationsDOIOpen Access PDF

Abstract

ABSTRACT: Among 281 patients with essential thrombocythemia and calreticulin (CALR) mutation, we found a variant allele frequency of ≥60% to be associated with significantly shortened myelofibrosis-free survival, mostly apparent with CALR type-1 and CALR type-indeterminate mutations.

Topics & Concepts

Essential thrombocythemiaMyelofibrosisCalreticulinMutationPolycythemia veraMedicineInternal medicineGeneticsBiologyGeneBone marrowEndoplasmic reticulumMyeloproliferative Neoplasms: Diagnosis and TreatmentKruppel-like factors researchChronic Myeloid Leukemia Treatments