Antisense oligonucleotides for neurodegeneration
Blair R. Leavitt, Sarah J. Tabrizi
Abstract
Promising clinical results for Huntington's disease give hope for other diseases
Topics & Concepts
NeurodegenerationOligonucleotideHuntington's diseaseDiseaseBiologyComputational biologyMedicineGeneticsGenePathologyGenetic Neurodegenerative DiseasesNeurogenetic and Muscular Disorders ResearchMitochondrial Function and Pathology