Viltolarsen: First Approval
Sohita Dhillon
Topics & Concepts
Exon skippingDystrophinMedicineDuchenne muscular dystrophyExonMorpholinoMuscular dystrophyBioinformaticsGeneticsInternal medicineAlternative splicingGeneBiologyZebrafishMuscle Physiology and DisordersProsthetics and Rehabilitation RoboticsRNA Research and Splicing