Cost-effectiveness of spinal muscular atrophy newborn screening based on real-world data in Belgium
Tamara Dangouloff, Praveen Thokala, Matthew D Stevenson, Nicolas Deconinck, Adele D’Amico, Aurore Daron, Stéphanie Delstanche, Laurent Servais, Mickaël Hiligsmann
Topics & Concepts
MedicineNewborn screeningSpinal muscular atrophyCost effectivenessQuality of life (healthcare)PediatricsQuality-adjusted life yearAtrophyPhysical therapyInternal medicineDiseaseRisk analysis (engineering)NursingNeurogenetic and Muscular Disorders ResearchCongenital Anomalies and Fetal SurgeryFamily and Disability Support Research