Long-term effects of eliglustat on skeletal manifestations in clinical trials of patients with Gaucher disease type 1
Timothy M. Cox, Joel Charrow, Elena Lukina, Pramod K. Mistry, Meredith C. Foster, Michel Peterschmitt
Topics & Concepts
MedicineEnzyme replacement therapyDiseaseClinical trialSurgeryInternal medicineLysosomal Storage Disorders ResearchTrypanosoma species research and implicationsGlycogen Storage Diseases and Myoclonus