Litcius/Paper detail

Rational design of cationic lipids for siRNA delivery

Sean C. Semple, Akin Akinc, Jianxin Chen, Ammen P. Sandhu, Barbara L. Mui, Connie K Cho, Dinah W.Y. Sah, Derrick Stebbing, Erin Crosley, Ed Yaworski, Ismail M. Hafez, J. Robert Dorkin, June Qin, Kieu Lam, Kallanthottathil G. Rajeev, Kim F. Wong, Lloyd B. Jeffs, Lubomir V. Nechev, Merete L. Eisenhardt, Muthusamy Jayaraman, Mikameh Kazem, Martin A. Maier, Masuna Srinivasulu, Michael J Weinstein, Qingmin Chen, Rene Alvarez, Scott Barros, Soma De, Sandra K. Klimuk, Todd Borland, Verbena Kosovrasti, William Cantley, Ying K. Tam, Muthiah Manoharan, Marco A. Ciufolini, Mark A. Tracy, Antonin de Fougerolles, Ian MacLachlan, Pieter R. Cullis, Thomas D. Madden, Michael J. Hope

2010Nature Biotechnology1,782 citationsDOI

Topics & Concepts

Cationic polymerizationIn vivoGene silencingRational designNucleic acidSmall interfering RNAChemistryBiochemistryLipid metabolismGene deliveryRNACell biologyBiophysicsPharmacologyTransfectionBiologyGeneBiotechnologyOrganic chemistryGeneticsRNA Interference and Gene DeliveryAdvanced biosensing and bioanalysis techniquesMicroRNA in disease regulation