Therapeutic Approaches for Duchenne Muscular Dystrophy: Old and New
Samuel Mackenzie, Stefan Nicolau, Anne M. Connolly, Jerry R. Mendell
Topics & Concepts
Duchenne muscular dystrophyDystrophinMedicineMuscular dystrophyPrednisoneDiseaseBioinformaticsMuscle diseaseGenetic enhancementCardiomyopathyRespiratory failureIntensive care medicineGeneInternal medicineGeneticsHeart failureBiologyMuscle Physiology and DisordersCardiomyopathy and Myosin StudiesNeurogenetic and Muscular Disorders Research