CRISPR-Cas9 In Vivo Gene Editing for Transthyretin Amyloidosis
Alan Solomon
Topics & Concepts
CRISPRGenome editingMedicineTransthyretinAmyloidosisGeneComputational biologyIn vivoGeneticsBioinformaticsPathologyBiologyAmyloidosis: Diagnosis, Treatment, OutcomesRenal Diseases and GlomerulopathiesCellular transport and secretion