Optimization of lipid nanoparticles for gene editing of the liver via intraduodenal delivery
Yining Zhu, Shuting Cai, Jingyao Ma, Leonardo Cheng, Christine Wei, Ataes Aggarwal, Wu Han Toh, Charles Shin, Ruochen Shen, Jiayuan Kong, Alan Mao, Yeh‐Hsing Lao, Kam W. Leong, Hai‐Quan Mao
Topics & Concepts
Gene knockdownGene deliveryGenetic enhancementReporter geneGenome editingBiologyPharmacologyComputational biologyGeneGene expressionMedicineBiochemistryCRISPRRNA Interference and Gene DeliveryCRISPR and Genetic EngineeringVirus-based gene therapy research