Litcius/Paper detail

Split intein-mediated protein trans-splicing to express large dystrophins

Hichem Tasfaout, Christine L. Halbert, Timothy S. McMillen, James M. Allen, Theodore R. Reyes, Galina Flint, Dirk Grimm, Stephen D. Hauschka, Michael Regnier, Jeffrey S. Chamberlain

2024Nature59 citationsDOIOpen Access PDF

Topics & Concepts

InteinRNA splicingTrans-splicingProtein splicingGeneticsComputational biologyBiologyCell biologyGeneRNAMuscle Physiology and DisordersViral Infectious Diseases and Gene Expression in InsectsVirus-based gene therapy research