Nusinersen in adults with spinal muscular atrophy: new challenges
Eugenio Mercuri, Valeria Sansone
Topics & Concepts
Spinal muscular atrophyMedicineObservational studyAtrophyCohortCohort studyPhysical therapyDiseaseInternal medicineNeurogenetic and Muscular Disorders ResearchCongenital Anomalies and Fetal Surgery