Respiratory Needs in Patients with Type 1 Spinal Muscular Atrophy Treated with Nusinersen
Valeria Sansone, Alice Pirola, Emilio Albamonte, Marika Pane, Andrea Lizio, Adele D’Amico, Michela Catteruccia, Renato Cutrera, Claudio Bruno, Marina Pedemonte, Sonia Messina, Fabrizio Rao, Elisabetta Roma, Francesca Salmin, Giorgia Coratti, Alessandra Di Bari, Roberto De Sanctis, Maria Carmela Pera, Maria Sframeli, Marco Piastra, Francesco Macagno, Giuseppe Vita, Enrico Bertini, Eugenio Mercuri
Topics & Concepts
MedicineSpinal muscular atrophyRespiratory systemCohortCohort studyAtrophyNatural historyVentilation (architecture)Mechanical ventilationPediatricsNeuromuscular diseaseAnesthesiaSurgeryInternal medicineDiseaseMechanical engineeringEngineeringNeurogenetic and Muscular Disorders ResearchCraniofacial Disorders and TreatmentsSpinal Dysraphism and Malformations