Litcius/Paper detail

Males with sickle cell disease have higher risks of cerebrovascular disease, increased inflammation, and a reduced response to hydroxyurea

Margherita Di Mauro, Sara El Hoss, Amina Nardo‐Marino, Sara Stuart‐Smith, John Strouboulis, John S. Gibson, David C. Rees, John Brewin

2023American Journal of Hematology11 citationsDOIOpen Access PDF

Abstract

Biological sex is important. Male sex is associated with worse outcomes in most measures, including cerebrovascular disease, hospital admissions, and blood transfusions, but not survival. Females also appear to have a better response to hydroxyurea therapy, reduced markers of inflammation, and better liver function.

Topics & Concepts

MedicineDiseaseCohortInternal medicineClinical trialCohort studyBioinformaticsOncologyImmunologyBiologyHemoglobinopathies and Related DisordersIron Metabolism and DisordersPrenatal Screening and Diagnostics