Long-term efficacy and safety of luspatercept for the treatment of anaemia in patients with transfusion-dependent β-thalassaemia (BELIEVE): final results from a phase 3 randomised trial
Maria Domenica Cappellini, Vip Viprakasit, Pencho Georgiev, Thomas D. Coates, Raffaella Origa, Abderrahim Khélif, Hong-Keng Liew, Adisak Tantiworawit, Lee-Ping Chew, Abdalla Khalil, P. Joy Ho, Kevin H.M. Kuo, Natalia Holot, Martina Perin, Ana Carolina Giuseppi, Wen‐Ling Kuo, Yinzhi Lai, Loyse Felber Medlin, Luciana Moro Bueno, Antonis Kattamis, Alì Taher
Topics & Concepts
MedicineAnemiaTerm (time)Blood transfusionThalassemiaPediatricsIntensive care medicineRandomized controlled trialSurgeryInternal medicineQuantum mechanicsPhysicsHemoglobinopathies and Related DisordersBlood groups and transfusionBlood transfusion and management